FREQUENTLY
ASKED
QUESTIONS

Below are answers to common questions about EMFLAZA® and starting TREATMENT

Is there a specific age range for which EMFLAZA may be used?

EMFLAZA is approved for use in patients with Duchenne muscular dystrophy who are 2 years of age and older.

Is it safe for my 2- to 5-year-old to take EMFLAZA even though the oral suspension contains benzyl alcohol?

EMFLAZA oral suspension can be safely prescribed to children 2 years of age and older. The amount of benzyl alcohol that a 2-year-old would receive with EMFLAZA oral suspension is less than the amount recommended as “safe” by the World Health Organization as a food additive. Other sources of benzyl alcohol used in combination with EMFLAZA should be monitored and discussed with your child’s healthcare provider.

What do I need to know about EMFLAZA and my child’s immunizations?

Before taking EMFLAZA, it is important that your child has received all immunizations according to immunization guidelines. For certain vaccines (live or live-attenuated vaccines), your child will need to wait 4 to 6 weeks prior to starting EMFLAZA.

Can I get EMFLAZA at my local pharmacy where I get all my other prescriptions?

EMFLAZA is not available at local pharmacies. It is a prescription medication available only through a specialty pharmacy. EMFLAZA is delivered right to your door through a PTC Therapeutics specialty pharmacy partner.

How much does EMFLAZA cost?

Once your healthcare provider has made the decision to prescribe EMFLAZA, your specialty pharmacy will do a benefit verification with your insurance company to identify your out-of-pocket costs related to EMFLAZA. Call PTC Cares™ at 1-844-4PTC-CARES (1-844-478-2227) to learn about your eligibility options.

If I have questions about how to take EMFLAZA, where can I get answers?

Please review the complete Instructions for Use and Prescribing Information for more information. If you have trouble finding what you need, you can also contact your loved one’s healthcare provider or PTC Cares™ for assistance.

Can my child stop taking EMFLAZA at any time?

Do not stop giving your child EMFLAZA without first consulting his healthcare provider. EMFLAZA should be taken once a day, every day, unless otherwise directed by a healthcare provider.